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核酸药物作为新兴治疗手段,通过调控基因表达治疗疾病,展现高效低毒优势,尤其在罕见病领域取得突破,正拓展至常见病。全球核酸药物市场快速增长,受适应症扩大、政策支持及研发合作驱动。预计未来,随着技术创新与资本投入增加,核酸药物行业将持续扩容,有望成为第三大类药物类别,推动医疗健康领域革新。